BioMarin focusses on developing first-in-class and best-in-class therapeutics that provide meaningful advances to patients who live with serious and life-threatening rare genetic diseases. BioMarin remains steadfast to its original mission to bring new treatments to market that will make a big impact on small patient populations.
BioMarin has a dedicated and professional approach to researching and understanding the potential of gene therapy. This video details how hard our team works to continue the advancement of gene therapy research for rare diseases.
For any questions contact BioMarin Medical Information at medinfo@bmrn.com.